Gene Therapy Restores Hearing In Majority Of Patients With Rare Deafness
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Researchers in a recent U.S. clinical trial say gene therapy restored hearing for most patients with a rare inherited deafness. The therapy delivers a working copy of the faulty gene to cells in the inner ear, aiming to correct the genetic cause and restore function. NPR reports the treatment produced lasting improvements for most patients several months after dosing, suggesting durable benefit rather than a short-lived effect.